BioPontis Alliance for Rare Diseases is a non-profit corporation dedicated to the development of new therapeutic agents to treat rare diseases. The niche philanthropy uses a collaborative approach, partnering with patient organizations and academic researchers. BioPontis provides the plans and executes the preclinical translational scientific, early clinical development, patenting, and business relationship management. We bring the expertise that is needed to advance ideas for treatments into drug compounds that are ready for uptake by the biopharmaceutical and biotech industry. BioPontis Alliance for Rare Diseases is a global non-profit development hub, inviting corporate, private and foundation philanthropic support to address a global community of people affected with rare diseases whose health needs are too often neglected as ‘too rare to care.’